Synaptix Bio ASO clinical trial update

Synaptix Bio has shared updates on the trial status. Although nothing is ever set in stone, they hope to start the trial in the UK in late 2025/early 2026 followed by the US.

CHOP continues to refine their natural history study to assist with the trial. We ask patients to use this link to participate in the survey https://redcap.chop.edu/surveys/?s=7MHM9TYHK9